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NORD Webinar – The Science Behind Gene Therapy

September 25, 2019 @ 3:00 pm - 4:00 pm

After decades of research and development, gene therapy is becoming a clinical reality in the US. With the first gene therapies already approved and many more in the pipeline, healthcare providers may soon gain the ability to treat more rare conditions.

To address this exciting topic, NORD is hosting a 5-part series on gene therapy. In part-2 of the series, The Science Behind Gene Therapy, we will explore how gene therapies are developed, the ways in which evidence-based science guides manufacturers of gene therapies, how vectors deliver gene therapies to the cells and what happens inside the body after gene therapy is delivered.We will cover these topics and more in this free webinar on September 25.

This webinar is perfect for patients, caregivers, advocates, students and the public.

Webinar Speakers:

Sven Kili, MD, Principal at Sven Kili Consulting Ltd., provides strategic consulting services to regenerative medicine companies.

Tiffany Lucas, PhD is an FDA Product Reviewer in the Division of Gene Therapy in the Center for Biologics Evaluation and Research (CBER).
Katie Kowalski, MPH is the Senior Manager for NORD’s Educational Initiatives.

Gene Therapy Webinar Series

The Science Behind Gene Therapy is the second webinar in an exciting five-part series on gene therapy from NORD in collaboration with the American Society for Gene and Cell Therapy (ASGCT.) Join us for upcoming topics in the series include the following.

  • Gene Therapy: Yesterday, Today and Tomorrow – Watch the archived video here.
  • The Science Behind Gene Therapy – Watch the archived video here.
  • The FDA’s Role in Gene Therapy – Watch the archived video here.
  • Understanding the Gene Therapy Process and Aftercare – Wednesday, November 20
  • Life After Gene Therapy – Wednesday, December 18

NORD thanks AVROBIO, Amicus, Bluebird Bio and Sarepta for their support of this educational resource.