Published December 9, 2021
Resource Library Search Results
Published June 25, 2021
Advancing Research Through the Global PNH Patient Registry
Published June 21, 2021
Continuing the Conversation: FDA and CDC Leaders Discuss the COVID-19 Pandemic and Vaccines
Published April 27, 2021
Transitioning to Adult Care
Published January 22, 2021
Advantages of the HOME Study for Metachromatic Leukodystrophy
Published September 4, 2020
Screen Baby Screen: Perspectives on Newborn Screening
Published June 27, 2020
Drug Supply in the Time of COVID-19
Published April 23, 2020
Called to Action: NORD’s Response to COVID-19
Published February 26, 2020
Starting a Not-For-Profit Organization: You Can Do It, We Can Help
Published February 11, 2020
Your Voice Matters: How to Engage with the FDA
Published July 18, 2018
Gene Therapy: Your Questions Answered
Published January 10, 2020
Life After Gene Therapy
Published December 5, 2019
Understanding Gene Therapy Process and Aftercare
Published December 13, 2019
FDA’s Role in Gene Therapy
Published October 7, 2019
The Science Behind Gene Therapy
Published September 19, 2019
Gene Therapy Yesterday, Today and Tomorrow
Published August 6, 2019
Self-Advocacy and Care Coordination
Published June 26, 2019
Generic Drugs and Biosimilars
Published January 18, 2019
How to Make Your Health Insurance Work For You
Published November 14, 2018
Open Enrollment for Health Insurance
Published August 14, 2018
Emergency Medical Protocols 101: Stories & Tools for Effective Advocacy
Published May 23, 2018
Patient Registries: What They Are and How to Start One
Published May 4, 2022
Post-Transplant Lymphoproliferative Disease Externally-Led PFDD
Published November 12, 2021
Navigating Insurance, Social Security Disability & Patient Assistance Programs
Published November 22, 2021
