Arthur Caplan, M.D., Ph.D. Drs. William F. and Virginia Connolly Mitty Chair Director, Division of Medical Ethics NYU Langone Medical Center |
Ashanthi De Silva Patient The Mighty |
Carrie Koenig Families Program Manager Hemophilia Federation of America |
Christina Clark Batten Disease Support & Research Association |
Christopher Anselmo Patient Muscular Dystrophy Association |
Christopher P. Austin, M.D. Director NCATS, NIH |
Christopher Schelling CEO and Founder ACER Therapeutics |
Dave Dubinksi Incyte Pharmaceuticals |
Debbie Skolaski Texas State Ambassador NORD Rare Action Network |
Dragos Roman, M.D. Deputy Director, Division of Gastroenterology & Inborn Erros of Product, Office of New Drugs, CDER FDA |
Ellen Matloff, M.S., C.G.C. President and CEO My Gene Counsel |
Ellis Unger, M.D. Director, Office of Drug Evaluation--1, Office of New Drugs, CDER FDA |
Eric Racine VP Patient Advocacy Sanofi Genzyme |
Gabriel Low Patient Ride for Rare Diseases |
Harjot Randhawa Patient NORD Student Chapter Leader |
Helene Cederroth President Wilhelm Foundation |
Ilan Irony Director, Office of Orphan Product Development FDA |
Jaimie Vikery VP, Advocacy & Policy Cure SMA |
Janet Woodcock, M.D. Director, Center for Drug Evaluation and Research FDA |
Janis Sherwood Founder Fight ALD Adrenoleukodystrophy |
Jason Slotnik, J.D. Principal and Founding Member Health Policy Strategies, Inc. |
Jefferey Shuren, M.D., J.D. Director, Center for Devices and Radiological Health FDA |
Jen Melanson Patient |
Jhoanny Cardenas Florida State Co-Ambassador NORD Rare Action Network |
Jim Palma Executive Director TargetCancer Foundation |
John Hopper President/Executive Director Fibrolamellar Cancer Foundation |
Jonathan Jackson, Ph.D. Instructor in Neurology and Director, CARE Research Center Harvard Medical School, Massachusetts General Hospital |
Karlyne Reilly NCI |
Maria Kefalas, Ph.D. Founder The Calliope Joy Foundation |
Marius George Linguraru Principal Investigator Children's National Health System |
Margot Johnson VP, Rare Disease & Vaccines TA Lead Pfizer Inc |
Mark Fendrick, M.D. Professor, Department of Internal Medicine, University of Michigan; Professor, Department of Health Management and Policy, University of Michigan; Director, University of Michigan Center for Value-Based Insurance Design Institute for Healthcare Policy & Innovation, University of Michigan Internal Medicine |
Markus Peters, Ph.D. Chief Commercial Officer Agilis Biotherapeutics |
Melinda Bachini Advocacy Coordinator The Cholangiocarcinoma Foundation |
Monica Weldon President/CEO/Founder Bridge the Gap - SYNGAP Education and Research Foundation |
Oodaye Skukla Chief Data Scientist HVH Precision Analytics |
Pam Mace, RN. Executive Director and FMD Patient Fibromuscular Dysplasia Society of America |
Peter L. Saltonstall President and CEO NORD |
Peter Marks, M.D., Ph.D. Director, Center for Biologics Evaluation and Research FDA |
Pushkal Garg, M.D. Chief Medical Officer and Senior Vice President, Clinical Development Alnylam Pharmaceuticals |
Rachelle Dixon President/Co-Founder HSAN1E Society |
Richard Pazdur, M.D. Director, Oncology Center of Excellence FDA |
Sarah Mulcahey Director, Clinical Program Management Vertex Pharmaceuticals |
Scott Gottlieb, M.D. FDA Commissioner FDA |
Stephen Aselage CEO Retrophin, Inc. |
Susan McCune, M.D. Director, Office of Pediatric Therapeutics, Office of the Commissioner FDA |
Tanisha Carino, Ph.D. Executive Director FasterCures |
Tejashri Purohit-Sheth, M.D., F.A.C.A.A.I, C.Q.I.A., C.A.P.T., U.S.P.H.S. Director, Division of Clinical Evaluation and Pharmacology/Toxicology, Office of Tissue and Advanced Therapies, CBER FDA |
Taylor Kane Founder and CEO Remember the Girls |
William Gahl, Ph.D. Director, NIH Undiagnosed Diseases Program National Institutes of Health (NIH) |
