This Summit is designed for those stakeholders involved in the research, development, access and support of orphan products in the rare disease community. Researchers from academia; drug and device companies; patient organizations and advocates; policy experts and government organizations responsible for rare disease research and orphan product oversight take part in this in-depth and innovative Summit. Key areas of responsibility and focus include:
It’s a chance to connect…
Network with patients, advocates, policy leaders, regulators, industry executives and researchers. Hundreds of engaged participants in a multi-faceted and meaningful meeting, with dedicated networking time within a fun and relaxed setting.
It’s a chance to explore…
Customize your onsite experience by choosing from multiple concurrent sessions and breakout summits. Explore the vast array of posters, exhibits and presentations to discover some of the newest breakthroughs and advancements.
It’s a chance to advance…
Gain tangible content, critical updates and innovative ideas to take back to your work. Equip yourself with new knowledge that can advance the dial in rare disease research and orphan treatment access.
It’s a chance to inspire…
Real-life stories of patients and families impacted by rare diseases. Cutting-edge advancements in genetics, research, drug development, diagnosis, treatment and access. Visionary insights on the road ahead.
It’s a chance to transform lives…
Be with the brightest minds in the rare disease community to discover opportunities to transform good medicine into great treatments.