Written by on March 15, 2017
Rare Impact Award
Cynthia Tifft, M.D., Ph.D.
Dr. Cynthia Tifft is working to solve some of the nation’s toughest medical mysteries. As the Director of the Pediatric Undiagnosed Diseases Program at the National Institutes of Health, she and her team strive… Read More
Written by Jennifer Huron on November 29, 2016
We are excited to announce that U.S. lawmakers have finally reached an agreement on the 21st Century Cures Act, a game-changer for patients with rare diseases. This agreement comes more than one year after the House passed its original version of the bill. The first vote is expected to take place… Read More