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Archives for: August 31st, 2017

FDA Announces First Gene Therapy in U.S.

Written by Mary Dunkle on August 31, 2017

In an action the rare disease community has been eagerly awaiting, the Food and Drug Administration (FDA) has announced the first-ever approval of a gene therapy in the U.S. The product is Kymriah, and it is approved to treat certain children and young adults who have a cancer of blood… Read More

NORD Awards New Research Grants for Rare Disease Research

Written by Jennifer Huron on February 24, 2017
Requests for Proposals-sticky (1)

Washington, D.C.—February 24, 2017—The National Organization for Rare Disorders (NORD), the leading independent, nonprofit organization committed to the identification, treatment, and cure of rare disorders, has awarded seven new research grants to fund rare disease research.

Research grants awarded for 2016 Requests for Proposals include:

For the study of Alveolar Capillary… Read More

Raise Your Hand for Rare Disease Research

Written by Christina Jensen on February 3, 2017
lundbeck-rddus-nord-homepage

By raising your hand, you can show your support for the 30 million Americans with rare diseases.

Simply click here and Lundbeck will donate $1 to rare disease research (up to $10,000 for the campaign).  The donations will be added to a general research fund managed by NORD.  The campaign will run through the month of February in honor of Read More