Jeron Hill

More access to treatment and resources for patients who are new to the community and...

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Sam Curtis

I’d rather focus on the rare disease community than focus on my own rare condition...

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Stephanie Levin

I was diagnosed with Pompe Disease in February 2021. I’ve probably been symptomatic for about...

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Megan Davis

For physicians to be educated on scleroderma. We are not lazy, crazy, seeking attention! We...

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Sarah Foye

I envision a future where people with rare muscle disorders like titinopathy (caused by disease-causing...

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Cristina Rosa

I am an advocate for legislation pertaining to rare diseases and the parent of Juju,...

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Lisa Zaret

I would like more attention called to West Nile virus and the rarest manifestation, meningoencephalitis.

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Kala McWain

Better mental and psychosocial support for caregivers.

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Julie Garza

Mask mandates in all medical settings would make an enormous difference to immunosuppressed patients.

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Karen Quandt

The price of rare disease drugs is extremely high. How do we fix this problem?

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FRED FABRICANT

Hopefully government and private sources will soon have designated funds to help cure Rare Diseases.

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Amy Chapman

I wish for every rare person to have a medication or a cure.

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Jenni Ward

I would like to see a change in how our Social Security Administration evaluates disability.

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Rebekah Palmer

A big difference to me would be more assistance in occupation as an adult living...

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Kim Madden

Rare disease research should be a relay race where we're all carrying the same baton.

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Megan Freeman

I would love to see if there could be another clinical trial done for my...

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Ruth Hochheiser

Education of the medical community about Orthostatic Tremor, including primary care physicians and neurologists.

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Christine McGarvey

Streamline the diagnostic odyssey by improving awareness of rare diseases among the medical community.

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Raymond A Huml

I want more robust incentives for companies developing rare disease drugs, especially for ultra-rare diseases.

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Alicia Dwyer

I have Susac Syndrome. We need research, as not one organization is doing it.

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Tytina Sanders-Bey

Access to care and treatment for specific health challenges. Easier access to prescription medication. Perhaps...

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Tammy Jones

My vision is to make connections with Rare Patients, one way I believe I can...

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Lesley Bennett

Expand Newborn Screening (including rare epilepsies) and establish Rare Disease Advisory Councils in every state.

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Sofia Horan

I hope to tell more patients that there is a treatment and there is hope.

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Jhoanny Cardenas

It would be wonderful if there was more focus on Rare Diseases for medical students.

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Cindy Choudhary

I would reimagine a healthcare system that could help treat my illnesses and actually listen.

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Jeneva Stone

I am hopeful that Maryland, my state, will establish a Rare Disease Advisory Council this...

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Janet Wilson

If there’s a way for more families with the same genetic results to submit to...

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Kerri Engebrecht

My passion and my plea is for mental health care to be looked at seriously...

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