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RareEdu
®
– Online Learning Platform
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Resource Library
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Publications On Rare Disease
Patient stories
Read More
Living with a Rare Disease
Manage your care
Getting Help & Support
Managing Your Disease
We can help
How NORD Can Help
Speak To Someone at NORD
Rare Disease Center Of Excellence
Patient Assistance Programs
Explore Clinical Trials
Find A Patient Organization
Caregiver Resources
State Resource Center – Discover Local Resources
Community Support
Where to start
Rare Diseases Defined
Financial & Medical Assistance
Call Center & Information Services
Bringing Together Your Community
Mentoring organizations
NORD Member List
Start a Rare Disease Organization
Membership Program
Becoming Research Ready
Launching Registries & Natural History Studies
Patient-Focused Drug Development
Improving clinical care
Rare Disease Centers of Excellence
Continuing Medical Education (CME)
Partnering with the community
Corporate Council
National Partnerships
Global Parnerships
Diversity, Equity & Inclusion
Community Support
Learn More
Advancing Research
For patients
List of Rare Diseases
Gene Therapy for Rare Disease
Find Clinical Trials & Research Studies
For researchers
Request for Proposals
Research Grant Programs
Data Standards for Rare Diseases
For clinicians
Resources for Patients
Find a Rare Disease Care Center
Continuing Medical Education (CME)
Connect
IAMRARE
®
Program Powered by NORD
Rare Disease Cures Accelerator (RDCA-DAP)
Add Your Expertise
Featured publication
View More
Driving Policy
NORD policy and you
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Taking action
Join the Rare Action Network®
Policy & Advocacy Taskforce
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Advocate for Rare Disease Policies as a Health Care Professional
Join A Current Campaign.
Learn about our current policy goals
Get Involved
Raising awareness and funds with NORD
Do-It-Yourself NORD Fundraiser
Students for Rare
Sports & Fitness Fundraisers
Media Inquiries
In your community
Attend An Upcoming Event
Find a Rare Disease Patient Organization
Stay Informed With NORD’s Email Newsletter
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Gaucher Disease
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Gene Therapy: Your Questions Answered
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Genetic Testing for Rare and Undiagnosed Diseases
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Genome Editing 1 – What is Genome Editing
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Genome Editing 2 – What are the safety, ethical and cost concerns
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Genome Editing 3 – How do I participate and what is the role of patient organizations
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Genome Editing 4 – The approval process
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Glut 1 Deficiency Syndrome
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Granulomatosis with Polyangiitis, Brandon’s Story
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Hemophilia, Guillermo’s Story
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National Organization for Rare Disorders
