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Archives for: September 13th, 2022

2022 RDCA-DAP Workshop

Written by Valaree DonFrancesco on September 13, 2022

Registration is OPEN for the 2022 RDCA-DAP Workshop! Join us this September as we bring rare disease stakeholders together for next-level platform demonstrations and case studies, industry expert presentations, panel discussions, and more.

Register here:

Attendees of the 1.5-day workshop, including patients, providers, researchers, clinicians, biopharmaceutical companies, regulatory reviewers, and… Read More

A Conversation on Drug Development for Rare Diseases

Written by Mary Dunkle on July 7, 2022

Explore the five steps in drug development and discover new opportunities to get involved

More than 95% of rare disease patients lack an FDA-approved treatment for their condition. However, today there are more opportunities than ever before for patients, caregivers and patient organizations to play a key role in advancing R&D… Read More

Breaking Down Data Siloes: New Analytics Platform Sparks Opportunity for Rare Disease Field

Written by Valaree DonFrancesco on September 1, 2021

TUCSON, Ariz. and WASHINGTON, September 1, 2021 — For two years, Critical Path Institute (C-Path), the National Organization for Rare Disorders (NORD) and the U.S. Food and Drug Administration (FDA) have joined with others throughout the rare disease community to create a novel, best-in-class platform to accelerate rare disease treatment innovation.

On Read More