NORD Rare Disease Scientific Symposium

Rare disease breakthroughs require collaboration. Join a community of researchers, clinicians, industry leaders, and others at the NORD® Rare Disease Scientific Symposium to share knowledge, exchange ideas, and forge partnerships that advance progress for patients across all rare diseases.

The agenda will offer case study presentations, panel discussions, and extended audience Q&A on such topics as:

• Innovative Study Designs and Methods for Rare Disease Research
• Approaches to Address the Challenges of Small Trial Enrollment Numbers and Disease Heterogeneity
• Successes and Challenges of Global Clinical Trials
• Using Alternative and Real-World Data for Rare Disease Research
• Multi-Stakeholder Collaboration in Research
• Successful Strategies for Earlier Pediatric Inclusion in Clinical Trials