NORD is grateful to the following companies who are active members of the Corporate Council
Cabaletta Bio
Dante Labs
EdiGENE
Neurogene
Orna Therapeutics, Inc
Shape Therapeutics
Taysha Gene Therapies
Acceleron Pharma
Aeglea BioTherapeutics
Apellis Pharmaceuticals
Applied Therapeutics
argenx
Ascendis Pharma
Asklepion Pharmaceuticals, LLC
Atara Biotherapeutics
Audentes Therapeutics
AVROBIO
bluebirdbio
Blueprint Medicines
BridgeBio
Camurus
ChemoCentryx
Crisprtx
Cytokinetics, Inc.
Dicerna
Editas Medicine
Enzyvant
Helixmith
Insmed Incorporated
Kiniksa
LEO Pharma
Lysogene
MeiraGTx
Moderna Therapeutics
Momenta Pharmaceuticals
Neurocrine Biosciences
Orchard Therapeutics Ltd.
Orphazyme
Ovid Therapeautics
Passage Bio
Rallybio
REGENXBIO
Rocket Pharmaceuticals, Inc
Sangamo Therapeutics
Savara
Sigilon Therapeutics
Soligenix, Inc.
Viela Bio
X4 Pharmaceuticals
Zealand Pharma
AbbVie Pharmaceuticals
Acadia Pharmaceuticals
Actelion Pharmaceuticals
Agios Pharmaceuticals
Alexion Pharmaceuticals, Inc.
Alnylam Pharmaceuticals
Amgen
Amicus Therapeutics, Inc.
Amryt Pharma
Astellas
AstraZeneca
AveXis, Inc.
BioCryst
Biogen
BioMarin Pharmaceuticals, Inc.
Boehringer-Ingelheim Pharmaceuticals
Catalyst Pharmaceuticals
Chiesi Rare Diseases
CSL Behring
Daiichi Sankyo
Deciphera
Dompé
Eiger BioPharmaceuticals
Foundation Medicine
Genentech, Inc.
GlaxoSmithKline PLC
Global Blood Therapeutics, Inc.
Greenwich Biosciences, Inc
Harmony Biosciences, LLC
Horizon Therapeutics
Incyte Corporation
Ionis Pharmaceuticals
Ipsen
Mallinckrodt Pharmaceuticals
Novartis
Otsuka America Pharmaceutical, Inc.
Pfizer, Inc.
PTC Therapeutics
Recordati Rare Diseases
Regeneron
Rigel Pharmaceuticals
Sanofi Genzyme
Sarepta Therapeutics
Sobi
Spark Therapeutics
Strongbridge Biopharma
Takeda Oncology
Travere Therapeutics, Inc.
UCB Pharma
Vanda Pharmaceuticals Inc.
Vertex Pharmaceuticals Worldwide
Zogenix, Inc.
Biotechnology Industry Organization (BIO)
Children’s National Health System
Eversana
HPS Group LLC.
ICON
Illumina
Massachusetts Biotechnology Council (MassBio)
Medidata
Myriad Women’s Health
Optum Frontier Therapies
Parexel
PhRMA
Syneos Health