Rare Disease News

Glybera Becomes First-ever Gene Therapy Approved in Europe

Published November 2, 2012 by NORD

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According to a report on the BBC News web site today, the European Commission has — for the very first time anywhere in the Western world — given final approval …

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Creative Collaborations May Be Key to Reducing Chemotherapy Risks

Published October 31, 2012 by NORD

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My friend’s 18-year-old son died recently following a 6-month battle with acute myeloid leukemia. There are many different stories I could tell about Tucker’s experience that are all too familiar …

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Rare Disease News

Glybera Becomes First-ever Gene Therapy Approved in Europe

Creative Collaborations May Be Key to Reducing Chemotherapy Risks

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