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Home / Rare Disease News / Members / Guest Blogs

Rare Disease News

Guest Blog: The Power of Patient Advocacy in Drug Development

Published April 8, 2025 by NORD

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Education
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Members
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The FDA approval of the first treatment for Friedreich’s Ataxia (FA) on Rare Disease Day in 2023 marked a significant milestone for the estimated 5,000 people in the U.S. and …

Continue reading “Guest Blog: The Power of Patient Advocacy in Drug Development”

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