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NORD CEO Statement on FDA Draft Guidance for the Plausible Mechanism Framework for Individualized Genetic Therapies

Published February 24, 2026 by NORD

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NORD is encouraged by efforts to strengthen and clarify regulatory tools that advance rare disease treatments. For conditions with extremely small patient populations, where traditional clinical trials are difficult to …

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NORD CEO Statement: Navigating Proposed Policy Changes and Their Impact on Rare Disease Advocacy

Published February 14, 2025 by NORD

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There are several proposed policy changes occurring across government entities, many of which have the potential to impact the rare disease community. At the National Organization for Rare Disorders (NORD®), …

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