Rare Disease Resource Library

Researchers, RDCA-DAP, Research & Drug Development, Educational Video, Externally-Led Patient-Focused Drug Development, Webinar, Research,

October 17, 2022

How Will RDCA-DAP® Support Patient Focused Drug Development?

Forming a Foundation, Research Ready, Research & Registries, Medical Professionals, Patient & Caregiver, Researchers, Research & Drug Development, Educational Video, Webinar, Research,

October 14, 2022

Natural History Studies and Patient Registries

Medical Professionals, Patient & Caregiver, Patient Organizations, Research & Drug Development, Externally-Led Patient-Focused Drug Development, Membership, Research,

October 4, 2022

Voice of the Patient Report: Post-Transplant Lymphoproliferative Disorder

Advocates, Medical Professionals, Patient Organizations, Researchers, Legislative Advocacy, Research & Drug Development, PDF, Research,

September 28, 2022

Impact of the Orphan Drug Tax Credit

Advocates, Medical Professionals, Patient Organizations, Students & Volunteers, Legislative Advocacy, Research & Drug Development, PDF, Research,

Orphan Drugs in the U.S.: Exclusivity, Pricing and Treated Populations

Advocates, Patient Organizations, Researchers, Legislative Advocacy, Research & Drug Development, Collection, Research,

Study on Orphan Drug Costs and Use

Advocates, Medical Professionals, Patient Organizations, Researchers, Students & Volunteers, Legislative Advocacy, Research & Drug Development, PDF, Research,

Orphan Drug Costs and Expenditures

Advocates, Medical Professionals, Researchers, Research & Drug Development, Understanding Rare Disease, PDF, Research,

5 Myths about the Orphan Drug Act

Advocates, Medical Professionals, Patient Organizations, Researchers, Students & Volunteers, Research & Drug Development, PDF, Research,

Orphan Drug Trends in the U.S. in 2018

Advocates, Medical Professionals, Patient & Caregiver, Patient Organizations, Researchers, Students & Volunteers, Legislative Advocacy, Research & Drug Development, Infographic, Research,

Orphan Drug Act Fact Sheet