Rare Disease Resource Library

Advocates, Medical Professionals, Patient & Caregiver, Patient Organizations, Researchers, Gene Therapy, Collection, Educational Video,

November 3, 2022

Genome Editing 3 – How do I participate and what is the role of patient organizations?

Advocates, Medical Professionals, Patient & Caregiver, Patient Organizations, Researchers, Gene Therapy, Collection, Educational Video,

Genome Editing 2 – What are the safety, ethical and cost concerns

Advocates, Medical Professionals, Patient & Caregiver, Researchers, RDCA-DAP, Research & Drug Development, Educational Video, Webinar, Research,

October 27, 2022

What You Need to Know About the Rare Disease Cures Accelerator-Data and Analytics Platform

Advocates, Patient & Caregiver, Patient Organizations, Researchers, Students & Volunteers, Advocacy, RDCA-DAP, Research & Drug Development, Infographic, PDF, Education, Policy,

October 20, 2022

The Five Steps in Drug Development (Spanish version)

Advocates, Patient & Caregiver, Patient Organizations, Researchers, Students & Volunteers, Advocacy, RDCA-DAP, Research & Drug Development, Infographic, PDF, Education, Policy,

The Five Steps in Drug Development

Forming a Foundation, Governance, Advocates, Patient Organizations, Advocacy, Membership, PDF, Membership,

Business Plan Template & Example (Print Ready)

Governance, Advocates, Patient Organizations, Advocacy, Membership, PDF, Membership,

Basics of Nonprofit Advocacy

Advocates, Medical Professionals, Patient & Caregiver, Researchers, Gene Therapy, Collection, Education, Research,

October 17, 2022

Approved Cellular and Gene Therapy Products, FDA

Advocates, Medical Professionals, Patient & Caregiver, Researchers, Gene Therapy, Collection, Education, Research,

ASGCT Gene & Cell Therapy FAQs

Advocates, Medical Professionals, Patient & Caregiver, Researchers, Gene Therapy, Collection, Education, Research,

ASGCT Gene & Cell Therapy Glossary